Adult stem cells from bone marrow used to reverse a rare genetic disease

Adult stem cells from bone marrow have been used to reverse a rare genetic disease. Scientists at the Scripps Research Institute used a mouse model of cystinosis, a genetic disease that can afflict children as young as six months old, causes deteriorating kidney function and inevitable kidney failure. Stephanie Cherqui, the scientist who developed the mouse model, said that adult bone marrow stem cell therapy is particularly well suited as a potential treatment for cystinosis because these cells... Readmore

Stem Cell